# Recombinant Adeno-associated Virus Administration for Patients With Menkes Syndrome

> **NCT05507996** · EARLY_PHASE1 · TERMINATED · sponsor: **Kunming Hope of Health Hospital** · enrollment: 1 (actual)

## Conditions studied

- Menkes Syndrome

## Interventions

- **DRUG:** Recombinant adeno-associated virus administration

## Key facts

- **NCT ID:** NCT05507996
- **Lead sponsor:** Kunming Hope of Health Hospital
- **Sponsor class:** OTHER
- **Phase:** EARLY_PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** TERMINATED
- **Start date:** 2022-08-18
- **Primary completion:** 2022-11-23
- **Final completion:** 2022-11-23
- **Target enrollment:** 1 (ACTUAL)
- **Why stopped:** The PI decides to stop.
- **Last updated:** 2022-11-30


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05507996

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05507996, "Recombinant Adeno-associated Virus Administration for Patients With Menkes Syndrome". Retrieved via AI Analytics 2026-06-24 from https://api.ai-analytics.org/clinical/NCT05507996. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
