# A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia

> **NCT05515536** · PHASE3 · ACTIVE_NOT_RECRUITING · sponsor: **PTC Therapeutics** · enrollment: 130 (actual)

## Conditions studied

- Friedreich Ataxia

## Interventions

- **DRUG:** Vatiquinone

## Key facts

- **NCT ID:** NCT05515536
- **Lead sponsor:** PTC Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2022-12-08
- **Primary completion:** 2027-12-31
- **Final completion:** 2027-12-31
- **Target enrollment:** 130 (ACTUAL)
- **Last updated:** 2025-10-30


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05515536

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05515536, "A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia". Retrieved via AI Analytics 2026-06-23 from https://api.ai-analytics.org/clinical/NCT05515536. Licensed CC0.

---

*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*