# Natural History of Danon Disease

> **NCT05548855** · — · COMPLETED · sponsor: **Rocket Pharmaceuticals Inc.** · enrollment: 59 (actual)

## Conditions studied

- Danon Disease

## Interventions

- **PROCEDURE:** Heart Transplant
- **DEVICE:** Cardiac Assistive Device

## Key facts

- **NCT ID:** NCT05548855
- **Lead sponsor:** Rocket Pharmaceuticals Inc.
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2022-09-26
- **Primary completion:** 2023-10-31
- **Final completion:** 2023-10-31
- **Target enrollment:** 59 (ACTUAL)
- **Last updated:** 2023-11-21


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05548855

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05548855, "Natural History of Danon Disease". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT05548855. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
