Withdrawal of Tiratricol Treatment in Males With Monocarboxylate Transporter 8 Deficiency (MCT8 Deficiency)
Conditions
- Monocarboxylate Transporter 8 Deficiency
- Allan-Herndon-Dudley Syndrome
Interventions
- DRUG: Tiratricol
- DRUG: Placebo
Sponsor
Rare Thyroid Therapeutics International AB
Collaborators
- [object Object]
- [object Object]