Registry of Patients Diagnosed With Lysosomal Storage Diseases
Conditions
- Mucopolysaccharidosis I
- Mucopolysaccharidosis II
- Mucopolysaccharidosis IV A
- Mucopolysaccharidosis VI
- Mucopolysaccharidosis VII
- Pompe Disease Infantile-Onset
- Neuronopathic Gaucher Disease
- Wolman Disease
Interventions
- OTHER: There is no intervention
Sponsor
University of California, San Francisco