Safety and Efficacy of Encapsulated Allogeneic MPS-1 Therapy
NCT05665036
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
WITHDRAWN
Status
INDUSTRY
Sponsor class
Stopped
Sponsor developing new product
Conditions
MPS I
MPS1-S
MPS1-HS
Interventions
COMBINATION_PRODUCT:
SIG-005 (hIDUA Producing Spheres)
Sponsor
Sigilon Therapeutics, Inc.