ISP-001: Sleeping Beauty Transposon-Engineered B Cells for MPS I
NCT05682144
·
clinicaltrials.gov ↗
PHASE1
Phase
RECRUITING
Status
11
Enrollment
INDUSTRY
Sponsor class
Conditions
Mucopolysaccharidosis IH/S
Mucopolysaccharidosis IS
Interventions
BIOLOGICAL:
Autologous Plasmablasts (B cells)
Sponsor
Immusoft of CA, Inc.