Phase 1/2a for Safety, PK and PD of SQY51 in Paediatric and Adult Patients Duchenne Muscular Dystrophy
Conditions
- Duchenne Muscular Dystrophy
Interventions
- DRUG: Phase 1, SQY51
- DRUG: Phase 2a, SQY51 (cohort 1)
- DRUG: Phase 2a, SQY51 (cohort 2)
- DRUG: Phase 2a, SQY51 (cohort 3)
Sponsor
Sqy Therapeutics
Collaborators