# Natural History of SMA

> **NCT05755451** · — · RECRUITING · sponsor: **Fondazione Policlinico Universitario Agostino Gemelli IRCCS** · enrollment: 1200 (estimated)

## Conditions studied

- Muscular Atrophy, Spinal

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT05755451
- **Lead sponsor:** Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** RECRUITING
- **Start date:** 2018-06-21
- **Primary completion:** 2033-12-30
- **Final completion:** 2033-12-30
- **Target enrollment:** 1200 (ESTIMATED)
- **Last updated:** 2023-03-06

## Collaborators

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## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05755451

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05755451, "Natural History of SMA". Retrieved via AI Analytics 2026-05-26 from https://api.ai-analytics.org/clinical/NCT05755451. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
