SMN Circular RNAs as Potential Biomarkers for the Therapeutic Response to Nusinersen in Spinal Muscular Atrophy Patients
NCT05761262
·
clinicaltrials.gov ↗
UNKNOWN
Status
91
Enrollment
OTHER
Sponsor class
Conditions
Spinal Muscular Atrophy
Sponsor
Fondazione Policlinico Universitario Agostino Gemelli IRCCS