# An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.

> **NCT05765981** · EARLY_PHASE1 · RECRUITING · sponsor: **Shanghai Jiao Tong University School of Medicine** · enrollment: 6 (estimated)

## Conditions studied

- Aromatic L-amino Acid Decarboxylase (AADC) Deficiency

## Interventions

- **DRUG:** VGN-R09b

## Key facts

- **NCT ID:** NCT05765981
- **Lead sponsor:** Shanghai Jiao Tong University School of Medicine
- **Sponsor class:** OTHER
- **Phase:** EARLY_PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** RECRUITING
- **Start date:** 2023-01-30
- **Primary completion:** 2025-02-20
- **Final completion:** 2029-02-20
- **Target enrollment:** 6 (ESTIMATED)
- **Last updated:** 2023-03-13

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05765981

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05765981, "An Early Clinical Trial to Evaluate VGN-R09b for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency.". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT05765981. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
