# Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatments

> **NCT05768048** · — · RECRUITING · sponsor: **Fondazione Policlinico Universitario Agostino Gemelli IRCCS** · enrollment: 500 (estimated)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT05768048
- **Lead sponsor:** Fondazione Policlinico Universitario Agostino Gemelli IRCCS
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** RECRUITING
- **Start date:** 2022-11-28
- **Primary completion:** 2027-11-27
- **Final completion:** 2027-11-27
- **Target enrollment:** 500 (ESTIMATED)
- **Last updated:** 2023-03-14

## Collaborators

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## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05768048

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05768048, "Long Term Trajectories of SMA Patients Receiving or Not Disease-modifying Treatments". Retrieved via AI Analytics 2026-06-02 from https://api.ai-analytics.org/clinical/NCT05768048. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
