# A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)

> **NCT05768386** · — · ENROLLING_BY_INVITATION · sponsor: **BioMarin Pharmaceutical** · enrollment: 172 (estimated)

## Conditions studied

- Hemophilia A

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT05768386
- **Lead sponsor:** BioMarin Pharmaceutical
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** ENROLLING_BY_INVITATION
- **Start date:** 2023-01-01
- **Primary completion:** 2040-01
- **Final completion:** 2040-01
- **Target enrollment:** 172 (ESTIMATED)
- **Last updated:** 2026-01-12


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05768386

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05768386, "A Long-Term Follow-Up Study in Severe Hemophilia A Subjects Who Received BMN 270 in a Prior BioMarin Clinical Trial (270-401)". Retrieved via AI Analytics 2026-05-28 from https://api.ai-analytics.org/clinical/NCT05768386. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
