MAP THE SMA: a Machine-learning Based Algorithm to Predict THErapeutic Response in Spinal Muscular Atrophy
NCT05769465
·
clinicaltrials.gov ↗
UNKNOWN
Status
247
Enrollment
OTHER
Sponsor class
Conditions
Spinal Muscular Atrophy
Interventions
DRUG:
disease modifying treatments
Sponsor
Fondazione Policlinico Universitario Agostino Gemelli IRCCS