# A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

> **NCT05776472** · — · RECRUITING · sponsor: **Swedish Orphan Biovitrum** · enrollment: 200 (estimated)

## Conditions studied

- Paroxysmal Nocturnal Hemoglobinuria

## Interventions

- **DRUG:** Pegcetacoplan

## Key facts

- **NCT ID:** NCT05776472
- **Lead sponsor:** Swedish Orphan Biovitrum
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** RECRUITING
- **Start date:** 2023-06-26
- **Primary completion:** 2026-08-15
- **Final completion:** 2029-08-15
- **Target enrollment:** 200 (ESTIMATED)
- **Last updated:** 2025-05-14

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05776472

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05776472, "A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT05776472. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
