# Mucolipidosis Type IV Natural History Study

> **NCT05782387** · — · ACTIVE_NOT_RECRUITING · sponsor: **Massachusetts General Hospital** · enrollment: 50 (estimated)

## Conditions studied

- Mucolipidosis Type IV

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT05782387
- **Lead sponsor:** Massachusetts General Hospital
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2023-03-15
- **Primary completion:** 2028-09
- **Final completion:** 2028-09
- **Target enrollment:** 50 (ESTIMATED)
- **Last updated:** 2026-04-23


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05782387

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05782387, "Mucolipidosis Type IV Natural History Study". Retrieved via AI Analytics 2026-06-09 from https://api.ai-analytics.org/clinical/NCT05782387. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
