# Orphan Drugs for Inherited Metabolic Diseases

> **NCT05818566** · — · COMPLETED · sponsor: **University of Lausanne** · enrollment: 39 (actual)

## Conditions studied

- Inborn Errors of Metabolism

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT05818566
- **Lead sponsor:** University of Lausanne
- **Sponsor class:** OTHER
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2022-10-01
- **Primary completion:** 2024-05-01
- **Final completion:** 2024-10-01
- **Target enrollment:** 39 (ACTUAL)
- **Last updated:** 2024-12-04


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05818566

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05818566, "Orphan Drugs for Inherited Metabolic Diseases". Retrieved via AI Analytics 2026-07-13 from https://api.ai-analytics.org/clinical/NCT05818566. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
