Study of the Selective GlyT1 Inhibitor Bitopertin for Steroid-Refractory Diamond-Blackfan Anemia
NCT05828108
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
COMPLETED
Status
15
Enrollment
NIH
Sponsor class
Conditions
Steroid-refractory Diamond-Blackfan Anemia (DBA)
Interventions
DRUG:
Bitopertin
Sponsor
National Heart, Lung, and Blood Institute (NHLBI)