Hematological Response in Patients With Paroxysmal Nocturnal Hemoglobinuria Treated With Anti-C5 Antibody: an External Control Arm Study for Iptacopan Use in Anti-C5 naïve Patients
Conditions
- Paroxysmal Nocturnal Hemoglobinuria
Interventions
- OTHER: Anti-C5 antibody treatment
Sponsor
Assistance Publique - Hôpitaux de Paris
Collaborators