Gene Therapy in Subjects With Biallelic RPE65 Mutation-associated Retinal Dystrophy
Conditions
- Biallelic RPE65 Mutation-associated Retinal Dystrophy
Interventions
- GENETIC: FT-001 Low Dose
- GENETIC: FT-001 Mid Dose
- GENETIC: FT-001 High Dose
Sponsor
Frontera Therapeutics