A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
NCT05861986
·
clinicaltrials.gov ↗
PHASE4
Phase
RECRUITING
Status
28
Enrollment
INDUSTRY
Sponsor class
Conditions
Muscular Atrophy, Spinal
Interventions
DRUG:
Risdiplam
Sponsor
Hoffmann-La Roche