Safety, Tolerability, PK and PD of ADX-038 in Healthy Participants and Paroxysmal Nocturnal Hemoglobinuria (PNH) Patients
Conditions
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
Interventions
- DRUG: ADX-038
- DRUG: Placebo
Sponsor
ADARx Pharmaceuticals, Inc.
Collaborators
- [object Object]
- [object Object]