A Phase 1, Dose Escalation Trial of RP-A601 in Subjects With PKP2 Variant-Mediated Arrhythmogenic Cardiomyopathy (PKP2-ACM)
NCT05885412
·
clinicaltrials.gov ↗
PHASE1
Phase
RECRUITING
Status
9
Enrollment
INDUSTRY
Sponsor class
Conditions
PKP2 Arrhythmogenic Cardiomyopathy (PKP2-ACM)
Interventions
GENETIC:
RP-A601
Sponsor
Rocket Pharmaceuticals Inc.