# Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency

> **NCT05911399** · — · AVAILABLE · sponsor: **Rare Thyroid Therapeutics International AB**

## Conditions studied

- Monocarboxylate Transporter 8 Deficiency
- Allan-Herndon-Dudley Syndrome

## Interventions

- **DRUG:** Tiratricol

## Key facts

- **NCT ID:** NCT05911399
- **Lead sponsor:** Rare Thyroid Therapeutics International AB
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** EXPANDED_ACCESS
- **Status:** AVAILABLE
- **Start date:** —
- **Primary completion:** —
- **Final completion:** —
- **Target enrollment:** — (—)
- **Last updated:** 2026-05-05

## Collaborators

- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT05911399

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT05911399, "Expanded Access Program for Tiratricol in Patients With Monocarboxylate Transporter 8 Deficiency". Retrieved via AI Analytics 2026-06-01 from https://api.ai-analytics.org/clinical/NCT05911399. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
