A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study
ENROLLING_BY_INVITATION
Status
Conditions
- Duchenne Muscular Dystrophy
Interventions
- GENETIC: delandistrogene moxeparvovec
Sponsor
Sarepta Therapeutics, Inc.
Collaborators