A Long-term Safety Study in Brazilian Patients With a Diagnosis of Spinal Muscular Atrophy Treated With Zolgensma
NCT06019637
·
clinicaltrials.gov ↗
RECRUITING
Status
50
Enrollment
INDUSTRY
Sponsor class
Conditions
Spinal Muscular Atrophies
Interventions
OTHER:
Onasemnogene Abeparvovec
Sponsor
Novartis Pharmaceuticals