Study of Sodium Phenylbutyrate (ACER-001) for the Treatment of Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)
Stopped Study has been temporarily stopped until another study is completed. Data from the other study may inform changes to this study.
Conditions
- Medium-chain Acyl-CoA Dehydrogenase Deficiency
Interventions
- DRUG: Sodium phenylbutyrate
Sponsor
Jerry Vockley, MD, PhD
Collaborators