# Leber Congenital Amaurosis Inherited Blindness of Gene Therapy Trial(LIGHT)

> **NCT06088992** · EARLY_PHASE1 · ACTIVE_NOT_RECRUITING · sponsor: **Xinhua Hospital, Shanghai Jiao Tong University School of Medicine** · enrollment: 9 (estimated)

## Conditions studied

- Leber Congenital Amaurosis

## Interventions

- **GENETIC:** HG004

## Key facts

- **NCT ID:** NCT06088992
- **Lead sponsor:** Xinhua Hospital, Shanghai Jiao Tong University School of Medicine
- **Sponsor class:** OTHER
- **Phase:** EARLY_PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** ACTIVE_NOT_RECRUITING
- **Start date:** 2023-01-10
- **Primary completion:** 2024-10-30
- **Final completion:** 2028-10-30
- **Target enrollment:** 9 (ESTIMATED)
- **Last updated:** 2024-09-19

## Collaborators

- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT06088992

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT06088992, "Leber Congenital Amaurosis Inherited Blindness of Gene Therapy Trial(LIGHT)". Retrieved via AI Analytics 2026-06-04 from https://api.ai-analytics.org/clinical/NCT06088992. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
