# Real-World Use of Novel Treatments in Patients With Spinal Muscular Atrophy (SMA): A Multi-Site Retrospective Chart Review of Pediatric SMA Patients Outside of the United States

> **NCT06178393** · — · COMPLETED · sponsor: **Novartis Pharmaceuticals** · enrollment: 162 (actual)

## Conditions studied

- Spinal Muscular Atrophy

## Interventions

_None listed._

## Key facts

- **NCT ID:** NCT06178393
- **Lead sponsor:** Novartis Pharmaceuticals
- **Sponsor class:** INDUSTRY
- **Phase:** —
- **Study type:** OBSERVATIONAL
- **Status:** COMPLETED
- **Start date:** 2022-05-05
- **Primary completion:** 2022-12-30
- **Final completion:** 2022-12-30
- **Target enrollment:** 162 (ACTUAL)
- **Last updated:** 2023-12-21


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT06178393

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT06178393, "Real-World Use of Novel Treatments in Patients With Spinal Muscular Atrophy (SMA): A Multi-Site Retrospective Chart Review of Pediatric SMA Patients Outside of the United States". Retrieved via AI Analytics 2026-06-03 from https://api.ai-analytics.org/clinical/NCT06178393. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*