A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)

NCT06192576 · clinicaltrials.gov ↗
RECRUITING
Status
10
Enrollment
INDUSTRY
Sponsor class

Conditions

Interventions

Sponsor

Sanofi

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