Evaluation of the Safety, Tolerability and Efficacy of a Gene Therapy Drug for the Treatment of Pediatric Fabry Disease
NCT06207552
·
clinicaltrials.gov ↗
EARLY_PHASE1
Phase
RECRUITING
Status
6
Enrollment
OTHER
Sponsor class
Conditions
Fabry Disease
Interventions
GENETIC:
BBM-F101 injection
Sponsor
Children's Hospital of Fudan University