A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4

NCT06246513 · clinicaltrials.gov ↗

PHASE3

Phase

ACTIVE_NOT_RECRUITING

Status

17

Enrollment

INDUSTRY

Sponsor class

Conditions

Limb-girdle Muscular Dystrophy

Interventions

BIOLOGICAL: SRP-9003
DRUG: Glucocorticoid

Sponsor

Sarepta Therapeutics, Inc.