Low-Dose Sirolimus to Increase Hematopoietic Function in Patients With RUNX1 Familial Platelet Disorder
NCT06261060
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clinicaltrials.gov ↗
PHASE2
Phase
RECRUITING
Status
6
Enrollment
OTHER
Sponsor class
Conditions
Familial Platelet Disorder
Hematopoietic
Interventions
DRUG:
Sirolimus
Sponsor
M.D. Anderson Cancer Center