Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease
NCT06270316
·
clinicaltrials.gov ↗
PHASE1,PHASE2
Phase
RECRUITING
Status
12
Enrollment
INDUSTRY
Sponsor class
Conditions
Fabry Disease
Interventions
DRUG:
AMT-191
Sponsor
UniQure Biopharma B.V.