A Study Comparing Two Doses of AGTC-501 in Male Participants With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (DAWN)
ENROLLING_BY_INVITATION
Status
Conditions
- X-Linked Retinitis Pigmentosa
Interventions
- BIOLOGICAL: AGTC-501 (high dose and standard corticosteroid regimen)
- BIOLOGICAL: AGTC-501 (low dose and standard corticosteroid regimen)
- BIOLOGICAL: AGTC-501 (high dose and modified corticosteroid regimen)
Sponsor
Beacon Therapeutics