# A Study of Sepiapterin in Participants With Phenylketonuria (PKU)

> **NCT06302348** · PHASE3 · RECRUITING · sponsor: **PTC Therapeutics** · enrollment: 56 (estimated)

## Conditions studied

- Phenylketonuria

## Interventions

- **DRUG:** Sepiapterin

## Key facts

- **NCT ID:** NCT06302348
- **Lead sponsor:** PTC Therapeutics
- **Sponsor class:** INDUSTRY
- **Phase:** PHASE3
- **Study type:** INTERVENTIONAL
- **Status:** RECRUITING
- **Start date:** 2024-03-04
- **Primary completion:** 2031-02-28
- **Final completion:** 2031-02-28
- **Target enrollment:** 56 (ESTIMATED)
- **Last updated:** 2026-05-06


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT06302348

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT06302348, "A Study of Sepiapterin in Participants With Phenylketonuria (PKU)". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT06302348. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*