A Long Term, Post-marketing Study of Immune Response in Patients Receiving Palynziq Treatment for PKU (PALisade)
NCT06305234
·
clinicaltrials.gov ↗
RECRUITING
Status
200
Enrollment
INDUSTRY
Sponsor class
Conditions
Phenylketonuria (PKU)
Interventions
DRUG:
Pegvaliase
Sponsor
BioMarin Pharmaceutical