Triheptanoin for Children With Primary-Specific Pyruvate Dehydrogenase Complex (PDC) Deficiency
NCT06340685
·
clinicaltrials.gov ↗
PHASE1
Phase
RECRUITING
Status
6
Enrollment
OTHER
Sponsor class
Conditions
Pyruvate Dehydrogenase Complex Deficiency
Interventions
DRUG:
Triheptanoin
Sponsor
Jirair Krikor Bedoyan
Collaborators
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