First in Human (FIH) Study of ALN-SOD in Adult Participants With Amyotrophic Lateral Sclerosis Associated With Mutation in the SOD1 Gene (SOD1-ALS)

NCT06351592 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

RECRUITING

Status

42

Enrollment

INDUSTRY

Sponsor class

Conditions

Amyotrophic Lateral Sclerosis (ALS)
Mutation in the Superoxide Dismutase-1 (SOD1) Gene

Interventions

DRUG: ALN-SOD
OTHER: Diluent
DRUG: Placebo (PB)

Sponsor

Regeneron Pharmaceuticals