Observational Study of Neurofilament Light Chain (NfL) as a Biomarker in Asymptomatic Carriers of the Transthyretin (TTR) Variants and Patients With Hereditary Transthyretin-mediated (hATTR) Amyloidosis With Polyneuropathy
Conditions
- Hereditary Amyloidosis, Transthyretin-Related
- Asymptomatic Carrier State
Interventions
Sponsor
Alnylam Pharmaceuticals