Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants With PNH Who Have Clinically Significant Extravascular Hemolysis
Conditions
- Paroxysmal Nocturnal Hemoglobinuria
- PNH
- Extravascular Hemolysis
Interventions
Sponsor
Alexion Pharmaceuticals, Inc.
Collaborators