# A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of JWK008 in Patients With Mucopolysaccharidosis Type I

> **NCT06519552** · PHASE1 · RECRUITING · sponsor: **West China Hospital** · enrollment: 6 (estimated)

## Conditions studied

- Mucopolysaccharidosis Type I

## Interventions

- **GENETIC:** JWK008 Single intravenous infusion administration

## Key facts

- **NCT ID:** NCT06519552
- **Lead sponsor:** West China Hospital
- **Sponsor class:** OTHER
- **Phase:** PHASE1
- **Study type:** INTERVENTIONAL
- **Status:** RECRUITING
- **Start date:** 2024-07-22
- **Primary completion:** 2026-06-22
- **Final completion:** 2029-06-22
- **Target enrollment:** 6 (ESTIMATED)
- **Last updated:** 2024-07-25


## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT06519552

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT06519552, "A Clinical Study Evaluating the Safety, Tolerability, and Initial Efficacy of JWK008 in Patients With Mucopolysaccharidosis Type I". Retrieved via AI Analytics 2026-06-01 from https://api.ai-analytics.org/clinical/NCT06519552. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*