Study of Sodium Phenylbutyrate (ACER-001) for the Treatment of Pediatric and Adults Patients With Medium Chain Acyl-CoA Dehydrogenase Deficiency (MCADD)

NCT06773026 · clinicaltrials.gov ↗

PHASE2

Phase

RECRUITING

Status

24

Enrollment

OTHER

Sponsor class

Conditions

Medium-chain Acyl-CoA Dehydrogenase Deficiency

Interventions

DRUG: Sodium phenylbutyrate

Sponsor

Jerry Vockley, MD, PhD

Collaborators

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