Study to Determine Optimal Dose and Evaluate Safety, Tolerability, and Pharmacokinetics of Progerinin in Patients With Hutchinson-Gilford Progeria Syndrome (HGPS)
ACTIVE_NOT_RECRUITING
Status
Conditions
- Hutchinson-Gilford Progeria Syndrome
Interventions
- DRUG: Progerinin
- DRUG: Lonafarnib
Sponsor
PRG Science & Technology Co., Ltd.