# A Basket Clinical Study to Assess Glycerol Tributyrate in Patients With Mitochondrial Encephalopathy, Lactic Acidosis, Stroke-like Episodes (MELAS) or Leber's Hereditary Optic Neuropathy-Plus (LHON-Plus)

> **NCT06792500** · PHASE1,PHASE2 · RECRUITING · sponsor: **George Washington University** · enrollment: 24 (estimated)

## Conditions studied

- MELAS Syndrome
- Lebers Hereditory Optic Neuropathy With Extra Ocular Symptoms (LHON-Plus)

## Interventions

- **DRUG:** Glycerol Tributyrate

## Key facts

- **NCT ID:** NCT06792500
- **Lead sponsor:** George Washington University
- **Sponsor class:** OTHER
- **Phase:** PHASE1,PHASE2
- **Study type:** INTERVENTIONAL
- **Status:** RECRUITING
- **Start date:** 2026-04
- **Primary completion:** 2027-10
- **Final completion:** 2027-10
- **Target enrollment:** 24 (ESTIMATED)
- **Last updated:** 2026-02-09

## Collaborators

- [object Object]
- [object Object]

## Primary source

ClinicalTrials.gov registry: https://clinicaltrials.gov/study/NCT06792500

## Citation

> US National Library of Medicine, ClinicalTrials.gov registration NCT06792500, "A Basket Clinical Study to Assess Glycerol Tributyrate in Patients With Mitochondrial Encephalopathy, Lactic Acidosis, Stroke-like Episodes (MELAS) or Leber's Hereditary Optic Neuropathy-Plus (LHON-Plus)". Retrieved via AI Analytics 2026-06-08 from https://api.ai-analytics.org/clinical/NCT06792500. Licensed CC0.

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*[Clinical trials dataset](/datasets/clinical-trials) · CC0 1.0*
