Personalized Antisense Oligonucleotide Therapy for A Single Participant With LMNB1 Mutation Associated Autosomal Dominant Leukodystrophy (ADLD)

NCT06816498 · clinicaltrials.gov ↗

PHASE1,PHASE2

Phase

ACTIVE_NOT_RECRUITING

Status

1

Enrollment

OTHER

Sponsor class

Conditions

Autosomal Dominant Leukodystrophy

Interventions

DRUG: nL-LMNB1-001

Sponsor

n-Lorem Foundation

Collaborators

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