Nucleoside Therapy in Patients With Telomere Biology Disorders
Conditions
- Telomere Biology Disorders
- Dyskeratosis Congenita
- Revesz Syndrome
- Hoyeraal Hreidarsson Syndrome
- Telomere Biology Disorders With Bone Marrow Failure
- Interstitial Lung Disease Due to Systemic Disease (Telomere Biology Disorder)
- Pulmonary Fibrosis, Familial (Telomere Biology Disorder)
Interventions
- DRUG: deoxycytidine
- DRUG: deoxythymidine
Sponsor
Suneet Agarwal