Single-Dose AAV-MECP2 Safety/Tolerability and Efficacy in Rett Syndrome
NCT06856759
·
clinicaltrials.gov ↗
EARLY_PHASE1
Phase
RECRUITING
Status
8
Enrollment
OTHER
Sponsor class
Conditions
Rett Syndrome
Interventions
GENETIC:
Intrathecal injection of AAV-MECP2 for the treatment of Rett syndrome
Sponsor
Guangzhou Women and Children's Medical Center