A Study to Assess the Efficacy and Safety of Weekly Doses of GLM101 in Participants With PMM2-CDG
ACTIVE_NOT_RECRUITING
Status
Conditions
- Phosphomannomutase 2 Deficiency
- PMM2-CDG
Interventions
- DRUG: GLM101 (Part A, Double-blind)
- DRUG: Placebo (Part A, Double-blind)
- DRUG: GLM101 (Part B, Open-label)
Sponsor
Glycomine, Inc.