Study to Assess the Pharmacokinetics, Safety, and Tolerability of Iptacopan in Pediatric PNH Patients
NCT06934967
·
clinicaltrials.gov ↗
PHASE3
Phase
RECRUITING
Status
12
Enrollment
INDUSTRY
Sponsor class
Conditions
Paroxysmal Nocturnal Hemoglobinuria (PNH)
Interventions
DRUG:
LNP023
Sponsor
Novartis Pharmaceuticals